Children in England with fatal condition to get world’s most expensive drug

Joe and Connie Elson, who were both found to have MLD. Joe was treated in a clinical trial of Libmeldy in Milan, but Connie did not meet the entry criteria and deteriorated. Photograph: Picasa/NHS England

Joe and Connie Elson, who were both found to have MLD. Joe was treated in a clinical trial of Libmeldy in Milan, but Connie did not meet the entry criteria and deteriorated. Photograph: Picasa/NHS England

source https://www.theguardian.com/society/2022/feb/04/children-in-england-with-fatal-condition-to-get-worlds-most-expensive-drug